Tiny engineered therapeutic delivery system safely solves genetic problems in mice: Nanomaterials show promise for treating hemophilia and cardiovascular disorder

Inserting genetic material into the body to treat diseases caused by gene mutations can work, scientists say - but getting those materials to the right place safely is tricky. Scientists now report that the lipid-based nanoparticles they engineered, carrying two sets of protein-making instructions, showed in animal studies that they have the potential to function as therapies for two genetic disorders.